Clinical Trial: A Retrospective Study to Characterize Participants With Propionic Acidemia

Study Status: RECRUITING
Recruit Status: RECRUITING
Study Type: OBSERVATIONAL

Official Title: A Retrospective Cohort Study to Characterize Propionic Acidemia Patients

Brief Summary: This is a non-interventional, global, multicenter, retrospective cohort study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).

Detailed Summary: This study will abstract participants data from their medical records from approximately 2015-2025.
All data will be abstracted retrospectively in 6-month increments.
Sponsor: ModernaTX, Inc.

Current Primary Outcome:

Original Primary Outcome:

Current Secondary Outcome:

Original Secondary Outcome:

Information By: ModernaTX, Inc.

Dates:
Date Received: March 03, 2023
Date Started: June 16, 2023
Date Completion: June 16, 2023
Last Updated: August 03, 2023
Last Verified: August 01, 2023